Intellia Therapeutics: NTLA-2002 CRISPR-based therapy reduces rates of Hereditary Angioedema (HAE) attacks
CRISPR gene editing based treatment reduced HAE attacks rates by up to 80%. NTLA-2002 was well tolerated by patients. The ...
Tag: CRISPR-Cas9
Gene editing improves photoreceptor function in CEP290-associated retinal degeneration
1. In this randomized controlled trial, among patients with centrosomal protein 290 (CEP290)-associated retinal degeneration, subretinal injection of EDIT-101 resulted ...
The Scan by 2 Minute Medicine®: UK Approves First CRISPR Treatment, Cardiac Considerations, Pelicans Player Has a Pneumothorax, and Life Expectancy Gaps
The Scan by 2 Minute Medicine® is a pop-culture medical newsletter and exclusive benefit for 2 Minute Medicine Plus subscribers. ...
![CRISPR-mediated gene activation rescues obesity caused by haploinsufficiency [PreClinical]](https://www.2minutemedicine.com/wp-content/uploads/2019/03/CRISPR-350x250.jpg)
CRISPR-Cas9 promoting fetal hemoglobin production improves severe sickle cell disease
1. In this randomized controlled trial, infusion of OTQ923 disrupted inhibitory HBG1 and HBG2 promoter regions of the gamma-globin gene. ...